Haemophilia gene therapy breakthrough

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Uploaded By: john . Added on: 12 December 2011.
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Description
A gene therapy study developed by Dr Amit Nathwani (UCL Cancer Institute) and colleagues in collaboration with St. Jude Children's Research Hospital, Memphis, Tennessee, has shown that adults with haemophilia B benefit from the treatment, reducing need for injections with clotting factor to prevent bleeds. The findings of the six-person study mark the first proof that gene therapy can reduce disabling, painful bleeding episodes in patients with the inherited blood disorder.

Further information:
http://www.ucl.ac.uk/news/news-articles/1112/111209-haemophilia-gene-therapy-study
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